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Norditropin has received orphan drug designation for the treatment of short stature associated with Noonan syndrome.
诺和诺德人体生长激素已经获得孤儿药指定,以治疗努南综合症引起的身材矮小.
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Up to 80 percent of children with Noonan syndrome suffer from significant short stature.
80%努南综合症患儿表现明显的身材矮小.
努南综合征???
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