About 80 people in Scotland would have been eligible for treatment with Ivacaftor, the trust estimates.

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The recent decision to make ivacaftor available in England is based on a discounted price that has not been offered to NHS Scotland.

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VX-661 was generally well-tolerated, both as monotherapy and in combination with ivacaftor, and most adverse events were mild to moderate in severity and similar between the treatment groups and those who received placebo.

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